Ongoing or Completed Trials & Studies
Enrolling/Ongoing:
Clinical and Genetic Studies in Spinal Muscular Atrophy
Metabolic Dysfunction in SMA: impact of nutritional management
Prospective Study of Bone Abnormalities in SMA
STOP SMA: Phenylbutyrate trial in pre-symptomatic infants with SMA
CARNI-VAL SMA Type I (multi-center) see www.projectcuresma.org
Study of Pediatric Motor Disorders
Completed:
Motor Unit Number Estimation in SMA
Pilot Trial of Valproic Acid in Spinal Muscular Atrophy
Pilot Trial of Sodium Phenylbutyrate in Spinal Muscular Atrophy
CARNI-VAL SMA TRIAL (multi-center) see www.projectcuresma.org
